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9PM
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20 September 2024 09:00 PM 10:00 PM
Tippi MacKenzie: Prenatal Stem Cell and Gene Therapies for Severe,Early-Onset Genetic DiseasesWe will discuss ongoing clinical trials and translational research to develop targeted therapies for fetuses with single gene disorders such as alpha thalassemia, lysosomal storage diseases, or spinal muscularatrophy. Speaker Institution: UCSF School of Medicine0 users have RSVPed :